North Star Assessment for limb-girdle type muscular dystrophies (NSAD)

Download scientific diagram | North Star Assessment for limb-girdle type muscular dystrophies (NSAD) person-item threshold distribution plot demonstrating good coverage of items for the population. The top histogram illustrates the abilities of the population, from the weakest on the left to the strongest on the right. The bottom histogram demonstrates a well-distributed range of items that test the ability of the population, with a ceiling for the individuals who were the very strongest and asymptomatic. from publication: Validation of the North Star Assessment for Limb-Girdle Type Muscular Dystrophies | Objective. The North Star Assessment for limb-girdle type muscular dystrophies (NSAD), a clinician-reported outcome measure (ClinRO) of motor performance, was initially developed and validated for use in dysferlinopathy, an autosomal recessive form of limb-girdle muscular | Muscular Dystrophy, Limb-Girdle Muscular Dystrophies and Neuromuscular Diseases | ResearchGate, the professional network for scientists.

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PDF] Assessment of disease progression in dysferlinopathy

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Muscular Dystrophy Association Singapore - Today is Limb-Girdle Muscular Dystrophy (LGMD) Awareness Day! Limb-girdle muscular dystrophies (LGMD) are a rare group of progressive genetic illnesses that usually affects the proximal muscles around